SPINRAZA (Nusinersen) is a prescription drug used to treat spinal muscular atrophy (SMA) in pediatric and adult patients. SMA is a rare genetic disease caused by a low level of protein in the motor neuron that are responsible for normal muscle functioning .The lack of protein causes motor neuron loss, progressive muscle weakness and may lead to premature death from respiratory failure. This is mostly observed among children and young adults. SPINRAZA increases the body’s ability to produce SMN protein critical to the health of motor neurons.
Manufacturer : Biogen Inc.